Citation
J Haem Pract 2015; 2(2):24-25. doi: 10.17225/jhp00057

Authors: David Perry

Doctor David Perry
Cambridge Haemophilia and Thrombophilia Centre, Cambridge University Hospitals NHS Foundation Trust Hills Road, Cambridge CB2 0QQ, UK. Email: david.perry@addenbrookes.nhs.uk

Abstract

Patients with haemophilia have benefited hugely from the advances in basic science achieved over the past 50 years. The introduction of clotting factor concentrates opened the door to home treatment and the subsequent availability of plasma and then recombinant products heralded the prophylaxis era. As clinicians and patients begin to manage the introduction of longer-acting factor concentrates, there are also many novel therapies and approaches in development, many of which offer the potential to transform the lives for individuals with inherited bleeding disorders and their families.

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